Gene Therapy for AP-4-associated Hereditary Spastic Paraplegia
Treatment for a rare disease, addressing the cause and aiming to be a single‑dose treatment for the lifetime of the patient
Published: 9th March 2021

Patents
- GB2005321.1 "Gene Therapy Treatment" Priority application filed 09/04/2020
IP Status
- Patent application submitted
Seeking
- Development partner
- Commercial partner
- Seeking investment